Publications scientifiques

Comprehensive analysis of the editing window of C-to-T TALE base editors

Maria Feola, Sylvain Pulicani, Diane Tkach, Alex Boyne, Robert Hong, Louisa Mayer, Aymeric Duclert, Philippe Duchateau & Alexandre Juillerat
Scientific Reports
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Non-viral DNA delivery and TALEN editing correct the sickle cell mutation in hematopoietic stem cells

Arianna Moiani, Gil Letort, Sabrina Lizot, Chloé Foray, Diane Le Clerre, Sonal Temburni-Blake, Patrick Hong, Sophie Leduc, Noémie Pinard, Alan Marechal, Eduardo Seclen, Alex Boyne, Louisa Mayer, Anne Chalumeau, Tristan Felix, Robert Hong, Sylvain Pulicani, Roman Galetto, Agnès Gouble, Marina Cavazzana, Alexandre JUillerat, Annarita Miccio, Aymeric Duclert, Philippe Duchateau & Julien Valton
Nature Communications
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TALEN-mediated intron editing of HSPCs enables transgene expression restricted to the myeloid lineage

Julien Valton, Philippe Duchateau, Alexandre Juillerat, Alex Boyne, Eduardo Seclen, Jessica C. Jang, Aminah O.Lawal, Sylvain Pulicani and Diane Tkach
Molecular Therapy
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Preclinical Evidence of an Allogeneic Dual CD20xCD22 CAR to Target a Broad Spectrum of Patients with B-cell Malignancies

Beatriz Aranda-Orgilles ; Isabelle Chion-Sotinel ; Jordan Skinner ; Steven Grudman ; Ben Mumford ; Chantel Dixon ; Jorge Postigo Fernandez ; Piril Erler ; Phillipe Duchateau ; Agnes Gouble ; Roman Galetto ; Laurent Poirot
Cancer Immunology Research
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Stromal depletion by TALEN-edited universal hypoimmunogenic FAP-CAR T cells enables infiltration and anti-tumor cytotoxicity of tumor antigen-targeted CAR-T immunotherapy

Shipra Das, Julien Valton, Philippe Duchateau, Laurent Poirot
Frontiers in Immunology
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